H201903 – HIV treatment with genetically modified T progenitors resistant to infection Isabelle André
N201902 – Quantitative measurement of antisense oligonucleotide effects on SMN transcript isoforms in spinal muscular atrophy Judith Melki
D201904 – Platform for the study of differentiation and cell dynamics during normal and pathological erythropoiesis Wassim El Nemer
D201903 – Functional validation by microfluidics of the gene therapy effect on sickle red blood cells Pierre Buffet
D201902 – Proteomic analysis of blood cells of sickle cell patients before and after gene therapy Patrick Mayeux
V201901 – CRX gene therapy in retinal dystrophies mouse models : proof of concept for CRX dominant mutations as well as CRX independent retinopathies Muriel Perron
N201901 – Live cell videomicroscopy of gene therapy tools in culture models of disease Mario Gomes Pereira
T201902 – Quality control of advanced therapy products and biological monitoring of patients post gene therapies Capucine Picard