N202001 – Circulating cell-free SMN RNAs as therapeutic monitoring biomarker in spinal muscular atrophy Judith Melki
T202001 – Donor-specific regulatory T cell therapy in transplantation through CAR engineering Julien Zuber
N202003 – Purchase of a Transmission Electron Microscope with a cryogenic object holder and of a Cryoplunger Bruno Saubaméa
N202004 – Therapeutic approaches by modulating mRNA splicing for the treatment of neuromuscular diseases Aurélie Goyenvalle
D202003 – Preclinical Studies for Genome-Editing based-Treatment of Sickle Cell Disease Annarita Miccio