AAVGene therapy Sanofi, WhiteLab Genomics, the TaRGeT Laboratory at Nantes University, and
Sanofi, WhiteLab Genomics, the TaRGeT Laboratory at Nantes University, and
Institut Imagine launch WIDGeT to make France a global leader in gene therapy
Gene therapygenome editingRed blood cellsSickle cell disease
Annarita Miccio receives 1st prize of the Paris Region Innovators Award 2023 for her work on hemoglobinopathies
Gene therapy
Accelerating gene therapy: assessment and prospects at the end of the DIM Gene Therapy program
Gene therapyInborn Errors of MetabolismMSUD
First in vivo success of a gene therapy for the maple syrup urine disease
Gene therapygenome editingRed blood cellsSickle cell disease
A new tool to correct a mutation in beta-thalassemia
Red blood cellsSickle cell disease
“The systematic screening of sickle cell disease extended to the entire French population is a real victory”
